Haemophilia is a rare, monogenic disease that occurs from a single gene mutation and can have debilitating effects on the individual. With two subtypes, this inherited condition is currently treated with lifelong coagulation factor replacement therapy but is an ideal candidate for gene therapy management.
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4 Mins
10th
December
EAHAD Presidential Interview: Flora Peyvandi
I love to do medicine, and I always wanted to do internal medicine-haematology, because I thought haematology was just facing up to blood…
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9 Mins
14th
August
Recent Advancements in wAIHA
AIHA is an acquired, heterogeneous group of rare diseases with a prevalence of 17 per 100,000.1 This group includes wAIHA…
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3 Mins
25th
July
Filgrastim Prophylaxis for Neutropenia in Myelodysplasia Pre-Surgery: Case Report
Myelodysplastic syndromes are a group of disorders that affect the bone marrow, subsequently affecting the growth and relative…
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